Lysogene Announces Presentations at Upcoming Scientific and Family Conferences

Lysogene Announces Presentations at Upcoming Scientific and Family Conferences 150 150 Lysogene

Presentations to Highlight Results from Natural History and Treatment Studies for MPS IIIA and IND-enabling studies in GM1 gangliosidosis

Paris, France and Cambridge, MA, US —March 22, 2019 at 07:30am CET— Lysogene (FR0013233475 – LYS), a leading, biopharmaceutical company pioneering gene therapy technologies to treat central nervous system diseases, today announced that data will be presented at several scientific and family events in the upcoming weeks.

47th European Society for Pediatric Neurology (SENP), Paris, France

  • Presentation: Design, baseline characteristics, and 2-year follow-up from the MPS IIIA natural history study used as control group in gene therapy trial
  • Presenter: Dr Bénédicte Heron, Hôpital Trousseau, Paris
  • Date: March 22, 2019
  • Time: 12:15-12:30pm CET

3rd Annual Gene Therapy for Rare Disorders, Boston MA, USA

  • Presentation: Navigating the Gene Therapy Path for CNS Diseases to the Clinic – Rationale, Pharmacology, and Delivery
  • Presenter: Dr Ralph Laufer, Lysogene
  • Date: March 27, 2019
  • Time: 11:45am EST

National Tay Sachs and Associated Diseases (NTSAD) 41st Annual Family Conference, Raleigh, NC

  • Research session: GM1 breakout
  • Presenter: Samantha Parker, Lysogene
  • Date : April 12, 2019
  • Time: 9:30-10:45am EST
About Lysogene

Lysogene is a gene therapy company focused on the treatment of orphan diseases of the central nervous system (CNS). The company has built a unique capability to enable a safe and effective delivery of gene therapies to the CNS to treat lysosomal diseases and other genetic disorders of the CNS. A pivotal clinical trial in MPS IIIA in partnership with Sarepta Therapeutics, Inc. is ongoing and a phase 1-2 clinical trial in GM1 Gangliosidosis is in preparation. In accordance with the agreements signed between Lysogene and Sarepta Therapeutics, Inc., Sarepta Therapeutics, Inc. will hold exclusive commercial rights to LYS-SAF302 in the United States and markets outside Europe; and Lysogene will maintain commercial exclusivity of LYS-SAF302 in Europe. Lysogene is also collaborating with an academic partner to define the strategy of development for the treatment of Fragile X syndrome, a genetic disease related to autism.


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Forward-Looking Statements

This press release may contain certain forward-looking statements, especially on the Company’s progress of its phase 2-3 clinical trial. Although the Company believes its expectations are based on reasonable assumptions, all statements other than statements of historical fact included in this press release about future events are subject to (i) change without notice,

(ii) factors beyond the Company’s control and (iii) the financial capabilities of the Company. These statements may include, without limitation, any statements preceded by, followed by or including words such as “target,” “believe,” “expect,” “aim,” “intend,” “may,” “anticipate,” “estimate,” “plan,” “objective”, “project,” “will,” “can have,” “likely,” “should,” “would,” “could” and other words and terms of similar meaning or the negative thereof. Forward-looking statements are subject to inherent risks and uncertainties beyond the Company’s control that could cause the Company’s actual results, performance or achievements to be materially different from the expected results, performance or achievements expressed or implied by such forward-looking statements. A further list and description of these risks, uncertainties and other risks can be found in the Company’s regulatory filings with the French Autorité des Marchés Financiers, including in the 2017 registration document (Document de référence), registered with the French Markets Authorities on June 4, 2018, under number R. 18-047, and future filings and reports by the Company. Furthermore, these forward-looking statements are only as of the date of this press release. Readers are cautioned not to place undue reliance on these forward-looking statements. Except as required by law, the Company assumes no obligation to update these forward-looking statements publicly, or to update the reasons actual results could differ materially from those anticipated in the forward-looking statements, even if new information becomes available in the future. If the Company updates one or more forward-looking statements, no inference should be drawn that it will or will not make additional updates with respect to those or other forward-looking statements.

This press release has been prepared in both French and English. In the event of any differences between the two texts, the French language version shall supersede.

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